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TREATMENT OF ARGINASE 1 DEFICIENCY

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TREATMENT OF ARGINASE 1 DEFICIENCY

PCT NATIONAL PHASE APPLICATION

Published

date

Filed on 7 November 2024

Abstract

A method of treating Arginase 1 (ARG1) deficiency (ARG1-D) in a subject, comprising administering a pegzilarginase to the subject, wherein the pegzilarginase is a pegylated human arginase 1 comprising a cobalt metal cofactor, and wherein the pegzilarginase is administered weekly at a dose of from about 0.05 mg/kg to about 0.2 mg/kg.

Patent Information

Application ID202447085472
Invention FieldCHEMICAL
Date of Application07/11/2024
Publication Number46/2024

Inventors

NameAddressCountryNationality
QUINN, Anthony G.c/o 805 Las Cimas Parkway Suite 100 Austin, Texas 78746U.S.A.U.S.A.

Applicants

NameAddressCountryNationality
IMMEDICA PHARMA ABSolnavaegen 3H 113 63 StockholmSwedenSweden

Documents

NameDate
202447085472-AMMENDED DOCUMENTS [14-11-2024(online)].pdf14/11/2024
202447085472-FORM 13 [14-11-2024(online)].pdf14/11/2024
202447085472-MARKED COPIES OF AMENDEMENTS [14-11-2024(online)].pdf14/11/2024
202447085472-COMPLETE SPECIFICATION [07-11-2024(online)].pdf07/11/2024
202447085472-DECLARATION OF INVENTORSHIP (FORM 5) [07-11-2024(online)].pdf07/11/2024
202447085472-DRAWINGS [07-11-2024(online)].pdf07/11/2024
202447085472-FIGURE OF ABSTRACT [07-11-2024(online)].pdf07/11/2024
202447085472-FORM 1 [07-11-2024(online)].pdf07/11/2024
202447085472-FORM 18 [07-11-2024(online)].pdf07/11/2024
202447085472-NOTIFICATION OF INT. APPLN. NO. & FILING DATE (PCT-RO-105-PCT Pamphlet) [07-11-2024(online)].pdf07/11/2024
202447085472-PRIORITY DOCUMENTS [07-11-2024(online)].pdf07/11/2024
202447085472-REQUEST FOR EXAMINATION (FORM-18) [07-11-2024(online)].pdf07/11/2024
202447085472-Sequence Listing in PDF [07-11-2024(online)].pdf07/11/2024
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